Neurology Clinical Studies

Some of the clinical trial opportunities available in Neurology are listed below along with summaries of various research registries and clinical database projects. Select a study to review a brief description and requirements. Parents or guardians of children who might be eligible for select studies are encouraged to talk with their neurologist about enrollment, as many studies only recruit patients already undergoing specific treatments.

Thank you for exploring these opportunities and helping us to find cures and prevent childhood disease.

Clinical Studies

Researchers

Childhood Absence Epilepsy Study

Childhood Absence Epilepsy: Rx PK-PD-Pharmacogenetics Study

Read more

Cough Study for Males with Neuromuscular Disease – Pilot

Cough Peak Flow And Airway Clearance in Pediatric Patients with Neuromuscular Disease

Read more

Dravet Syndrome Treatment with Lorcaserin – Phase III

Study with Open-Label Extension Phase of Lorcaserin as Adjunctive Treatment in Subjects with Dravet Syndrome

Read more

Duchenne Muscular Dystrophy and MP-104

Expanded Access Protocol Intended to Provide Treatment With MP-104 (deflazacort) to U.S. Children, Adolescents, and/or Adults with Duchenne Muscular Dystrophy

Read more

Duchenne Muscular Dystrophy and SRP-4045 and SRP-4053 – Phase III

Study With an Open-Label Extension to Evaluate the Efficacy and Safety of SRP-4045 and SRP-4053 in Patients with Duchenne Muscular Dystrophy

Read more

Duchenne Muscular Dystrophy and Treatment With PF-06252616 – Phase II

Study to Evaluate the Safety, Efficacy, and Pharmacodynamics of PF-06252616 in Ambulatory Boys With Duchenne Muscular Dystrophy

Read more

Duchenne Muscular Dystrophy Treatment With Ataluren – Phase III

Study Of Ataluren (PTC124) In Patients With Nonsense Mutation Dystrophinopathy

Read more

Duchenne Muscular Dystrophy Treatment With Eteplirsen – Phase III

Study with a Concurrent Untreated Control Arm to Evaluate the Efficacy and Safety of Eteplirsen in Duchenne Muscular Dystrophy

Read more

Epilepsy Rescue Therapy with USL261 Spray: The ARTEMIS-1 Study – Phase III

Study of the Safety and Efficacy of Intranasal Midazolam (USL261) in the Outpatient Treatment of Subjects with Seizure Clusters

Read more

Epilepsy Rescue Therapy with USL261 Over a Long-Term – Phase III

Study of USL261 in the Outpatient Treatment of Subjects with Seizure Clusters

Read more

Epilepsy Surgery Study

Retrospective Review of Pediatric Epilepsy Surgery Program

Read more

Epilepsy Therapy Using Brivaracetam with Other Medications – Phase III

Study to Evaluate the Safety and Efficacy of Brivaracetam Used as Adjunctive Treatment in Pediatric Subjects with Epilepsy

Read more

Establishing Cytokine Profiles in Patients with MS

Cytokine Profiles in Pediatric Multiple Sclerosis and Other Acute Demyelinating Disorders in Children

Read more

Migraine Treatment with Galcanezumab: The REBUILD-1 Study – Phase III

Study of Galcanezumab in Adolescent Patients 6 to 17 Years of Age with Episodic Migraine – the REBUILD-1 Study

Read more

Migraine Treatment with Galcanezumab: The REBUILD-2 Study – Phase III

Study of Galcanezumab in Adolescent Patients 12 to 17 Years of Age with Chronic Migraine – the REBUILD-2 Study

Read more

Saliva Test for Anti-Seizure Drug Levels in Infants

Phenobarbital Levels in Neonates: A Comparison Between Blood and Saliva Levels

Read more

Stroke Study and Database

Institutional and International Pediatric Stroke Study and Database

Read more