Advancing Hope: Pioneering Therapy for Rare Diseases

Feb. 19, 2016
8 a.m. to 6 p.m.
Children's Hospital of Pittsburgh of UPMC
John G. Rangos Sr. Conference Center
Pittsburgh, PA

Join us for this inaugural one-day conference to explore innovative therapies for children who are diagnosed with rare diseases. Connect with our distinguished panel of international experts.

Download the Advancing Hope: Pioneering Therapy for Rare Disease Brochure (PDF)

Live Video Streaming

The conference is free and available by live video stream. Only on-site participants will be eligible for CME credits. Attendees must register in advance in order to participate in the live broadcast.

To join our live video broadcast throughout the conference, please use the links provided below. 

Please note that live streaming is viewable by desktop and laptop computer, and Apple mobile devices only. (Android mobile devices are not enabled.) Also, for best viewing capabilities, please download and install the free Microsoft Silverlight plug-in.

For technical issues, please call customer support at 412-692-9465.

Keynote Speaker

Edwin Naylor, PhD, MPH
Expert in newborn screening
Adjunct Professor of Pediatrics (Genetics)
Medical University of South Carolina
2014 Recipient of the Robert Guthrie Award

Guest Speaker

Senator Robert P. Casey, Jr. Senator Robert P. Casey, Jr.
Sponsor of the Advancing Hope Act of 2015, which extends and strengthens the U.S. Food and Drug Administration’s priority review voucher program for rare, life-altering pediatric diseases, including all pediatric cancers and sickle cell disease. It also allows the program to continue indefinitely. 

Course Director

Jerry Vockley, MD, PhD Chief, Medical Genetics Director, Center for Rare Disease Therapy  Jerry Vockley, MD, PhD
Chief, Medical Genetics
Director, Center for Rare Disease Therapy
Children's Hospital of Pittsburgh of UPMC
Cleveland Family Professor of Pediatric Research
Professor of Human Genetics
University of Pittsburgh School of Medicine 

Registration

Online Registration 
Onsite attendance is limited. Please register by Feb. 15, 2016 to secure a seat. Registration is required for joining the live online broadcast. 

Sponsored by the Center for Rare Disease Therapy at Children's Hospital of Pittsburgh of UPMC and the University of Pittsburgh School of Medicine, Center for Continuing Education in the Health Sciences.

This activity has been approved for AMA PRA Category 1 Credit(s)TM

The University of Pittsburgh is an affirmative action, equal opportunity institution.

Agenda

Learn more about what to expect at the one-day conference and review the full Advancing Hope: Pioneering Therapy for Rare Diseases Agenda.

Accommodations

Springhill Suites by Marriott Bakery Square
134 Bakery Square Blvd.
Pittsburgh, PA 15206
412-362-8600

Courtyard by Marriott Shadyside/Oakland
5308 Liberty Avenue
Pittsburgh, PA 15224
412-683-3113