Lily Smith – Krabbe Disease

Learn more about Lily's experience with Krabbe Disease at Children's Hospital.

Watch Lily’s story and learn how her family is finding help and hope through the expertise of the Center for Rare Disease Therapy and the Blood and Marrow Transplant & Cellular Therapies at UPMC Children's Hospital of Pittsburgh.

See more patient stories from the Center for Rare Disease Therapy.

Contact Us

At the Center for Rare Disease Therapy, every child diagnosed with a rare disease receives an individualized treatment plan and family-centered care.

For an appointment, consult, or referral, contact us:

We’ll be in touch within 2 business days.

Cassidy suffered from Ewing's Sarcoma. Read more about her procedure and experience at UPMC Children's Hospital of Pittsburgh.
Read Cassidy's Story >>
Austin was diagnosed with sickle cell disease shortly after birth. He received a bone marrow transplant from his older brother at UPMC Children's Hospital of Pittsburgh.
Read Austin 's Story >>